The Latest Breaking News from Gene Therapy

Shares of SRPT stock launched Monday after FDA advisors voted late Friday in support of a highly anticipated gene therapy from Sarepta.

An estimated 295 million people suffer from visual impairment globally. Around 43 million of those people are living with blindness. While not every form of blindness can be cured, recent scientific breakthroughs have uncovered new ways to treat some forms of inherited blindness through gene therapy.

Gene therapies treat or prevent disease by tweaking the content or expression of cells' DNA.

In a surprise decision, the FDA will hold an advisory committee to discuss Sarepta's gene therapy, and SRPT stock tanked Friday.

A cure for a deadly spinal disorder will be given out on the NHS after pioneering gene therapy costing £1.8million was approved today for infants before symptoms begin

Scientists in Bristol have experimented with the therapy on mice and found it effectively rewound their hearts by the equivalent of 10 human years - soon they hope to use it on heart failure patients

Sarepta could snag an accelerated approval for its muscular dystrophy gene therapy, analysts suggested Wednesday as SRPT stock rocketed.

Teddi Shaw suffers from deadly metachromatic leukodystrophy and had her stem cells removed and the faulty genes replaced

'Without this treatment, we would be facing both our children being taken away'