The Latest Breaking News from Gene Therapy

A new type of gene therapy could be cheaper, safer, and more efficient at treating diseases like muscular dystrophy and sickle cell disease.

The U.S. Food and Drug Administration approved a gene therapy for dystrophic epidermolysis bullosa, also known as butterfly disease.

Gene therapy has helped doctors make major strides in treating inherited blindness, and it's now being explored for other conditions.

An estimated 295 million people suffer from visual impairment globally. Around 43 million of those people are living with blindness. While not every form of blindness can be cured, recent scientific breakthroughs have uncovered new ways to treat some forms of inherited blindness through gene therapy.