The Latest Breaking News from Gene Therapy

U.S. health regulators have approved a gene therapy for the most common form of hemophilia

All five people aboard the Titan are believed dead after an implosion. Saturday marks a year since the Supreme Court overturned Roe. The FDA approves the first gene therapy for muscular dystrophy.

A new type of gene therapy could be cheaper, safer, and more efficient at treating diseases like muscular dystrophy and sickle cell disease.

The U.S. Food and Drug Administration approved a gene therapy for dystrophic epidermolysis bullosa, also known as butterfly disease.

Gene therapy has helped doctors make major strides in treating inherited blindness, and it's now being explored for other conditions.

An estimated 295 million people suffer from visual impairment globally. Around 43 million of those people are living with blindness. While not every form of blindness can be cured, recent scientific breakthroughs have uncovered new ways to treat some forms of inherited blindness through gene therapy.

Nicola Kelleher's partner Bradley Benjamin has a hereditary kidney disease which has seen him suffer on dialysis for years - and they didn't want the same outcome for their child

The FDA is considering greenlighting the experimental treatment under its accelerated approvals program. Some critics point out the therapy isn't yet proven to work and may be costly.

A world-first trial at UCL and UCLH has found a new gene therapy for Alzheimer's disease that is able to safely lower levels of the harmful tau protein known to cause the disease. Read further on Dynamite News: