
A baby boy with a rare illness is making “incredible” progress after he became the first ever patient to receive a new gene therapy.
Fourteen-month-old Tomas was diagnosed with ornithine transcarbamylase (OTC) deficiency when he was a few weeks old.

A baby boy with a rare illness is making “incredible” progress after he became the first ever patient to receive a new gene therapy.
Fourteen-month-old Tomas was diagnosed with ornithine transcarbamylase (OTC) deficiency when he was a few weeks old.