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The Independent UK
The Independent UK
National
Matthew Perrone

Second patient death reported with gene therapy for muscular dystrophy

US Duchenne's Therapy Death - (Copyright 2016 The Associated Press. All rights reserved.)

Shares of Sarepta Therapeutics plunged Monday after the biotech drugmaker reported a second death in connection with its gene therapy for muscular dystrophy.

Sarepta reported the death over the weekend and provided additional details about its response, which includes pausing shipments of the therapy, Elevidys, for older patients who are no longer able to walk. The one-time treatment is approved for children with a genetic variant of Duchenne’s muscular dystrophy, which causes weakness, loss of mobility and early death in males.

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