PTC Therapeutics Could Challenge BioMarin For Metabolic Disorder Treatment On Saturday, BioMarin Pharmaceutical Inc. (NASDAQ:BMRN) released new Phase 3 PEGASUS study results on Saturday. Benzinga · Sep 8, 2025
PTC Therapeutics Faces FDA Rejection On Rare Disease Treatment Over Efficacy Concerns The U.S. Food and Drug Administration (FDA) issued a Complete Response Letter (CRL) on Tuesday related to PTC Therapeutics, Inc.‘s (NASDAQ:PTCT) New Drug Application (NDA) for vatiquinone for Friedreich’s ataxia. Benzinga · Aug 19, 2025
Sephience Gets FDA Approval, Now A Key Revenue Driver For PTC Therapeutics The U.S. Food and Drug Administration approved on Monday PTC Therapeutics, Inc.’s (NASDAQ:PTCT) SEPHIENCE (sepiapterin) for children and adult patients with phenylketonuria (PKU). Benzinga · Jul 29, 2025
These Analysts Increase Their Forecasts On PTC Therapeutics PTC Therapeutics, Inc. (NASDAQ:PTCT) announced it has gained FDA approval for SEPHIENCE on Monday. Benzinga · Jul 29, 2025
PTC Therapeutics Signs Exclusive Global License And Collaboration Agreement With Novartis; PTC To Receive Upfront Payment Of $1B, Up To $1.9B In Development, Regulatory And Sales Milestones PTC Therapeutics, Inc. (NASDAQ:PTCT) announced today the signing of an exclusive global license and collaboration agreement with Novartis Pharmaceuticals Corporation, a subsidiary of Novartis AG (NYSE:NVS), for its Benzinga · Dec 2, 2024
PTC Therapeutics Ends Utreloxastat Development After Rare Neurodegenerative Disease Trial Misses Goal, Analyst Maintains Outperform With Focus On Sepiapterin, Huntington's Programs PTC Therapeutics halts Utreloxastat development after ALS trial disappoints. Analysts highlight promising pipeline, including Huntington's and PKU programs. Benzinga · Nov 27, 2024
Chart of the Day: PTC Therapeutics (PTCT) Upgraded To Buy by Zacks The Chart of the Day belongs to the biopharmaceutical company PTC Therapeutics (PTCT) . I found the stock by using Barchart's powerful screening functions to find stocks with the highest technical buy signals, highest Weighted Alpha, superior current momentum and having a Trend Seeker buy signal then used the Flipchart... Barchart · May 18, 2023