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Benzinga

Business

Vandana Singh

PTC Therapeutics Could Challenge BioMarin For Metabolic Disorder Treatment

BioMarin PTC Therapeutics BioMarin Pharmaceutical Inc BMRN Pharmaceutical William Blair

Ptc,Therapeutics,Sign,,Logo,At,Pharmaceutical,Company,Office,-,Sunnyvale,

On Saturday, BioMarin Pharmaceutical Inc. (NASDAQ:BMRN) released new Phase 3 PEGASUS study results on Saturday.

The data show that its therapy Palynziq (pegvaliase-pqpz) significantly reduced blood phenylalanine (Phe) levels in adolescents with phenylketonuria (PKU), a rare metabolic disorder.

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Top stories on inkl right now

AI-driven disinformation running rampant on social media before US midterms, experts warn

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The Guardian - US

US bans vehicles from China’s BYD at Japan military base, calling them ‘unacceptable’ risk

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Court blocks bid by Trump DoJ to stop California from counting mail-in ballots

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One of the ‘Cornell 7’ wants the claims against him dismissed, arguing: ‘Essentially a lawsuit about a forced kiss’

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The Independent UK

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Finnish and Norwegian leaders hold rare ‘frank and substantive’ call with Putin on Ukraine – Europe live

Alexander Stubb and Jonas Gahr Støre say they discussed future negotiations to help to end the war, related to forthcoming talks in Abu Dhabi

The Guardian - UK

Colombian Rapper Chelo Hop's Israel Flag Stunt Exposes Political Divisions Behind Petro's Legacy

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Top stories on inkl right now

AI-driven disinformation running rampant on social media before US midterms, experts warn

Social media companies including Meta have pulled back on efforts to protect voters from election-meddling lies

The Guardian - US

US bans vehicles from China’s BYD at Japan military base, calling them ‘unacceptable’ risk

US military says the restrictions on the electric vehicles at Kadena airbase also apply to delivery drivers and taxis

The Guardian - AU

Court blocks bid by Trump DoJ to stop California from counting mail-in ballots

Newsom accuses Trump of ‘assault on democracy’ as DoJ claims 20,000 registered voters in state are non-citizens

The Guardian - US

One of the ‘Cornell 7’ wants the claims against him dismissed, arguing: ‘Essentially a lawsuit about a forced kiss’

Lawyers for Diego Sarabia say the allegations against him do not support Jane Doe’s broader accusations of rape and sexual assault

The Independent UK

One subscription that gives you access to news from hundreds of sites

Already a member? Sign in here

Finnish and Norwegian leaders hold rare ‘frank and substantive’ call with Putin on Ukraine – Europe live

Alexander Stubb and Jonas Gahr Støre say they discussed future negotiations to help to end the war, related to forthcoming talks in Abu Dhabi

The Guardian - UK

Colombian Rapper Chelo Hop's Israel Flag Stunt Exposes Political Divisions Behind Petro's Legacy

Chelo Hop's Israeli flag incident at a Bogotá music festival draws diplomatic criticism and renews debate over Colombia's political legacy

International Business Times UK

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2,000-year-old Roman emperor's marble torso sold for $34.26 million in October 2026

A stunning marble torso of a Roman emperor made headlines at an auction, fetching an astounding $34.26 million, breaking previous records. This remarkable piece, which was sold for only $7.36 million in 2010, showcases its enduring appeal. With its origins in ancient Rome, the sculpture highlights military honor and divine…

The Times of India

Fake Scarlett Johansson Quote? The Truth Behind Claims She Opposed LGBTQ Themes in Children's Cartoons

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International Business Times UK

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