New platform to transform care for millions of children with rare diseases

• A new platform called KidsRare is being developed to accelerate diagnoses and improve treatments for children in the UK living with rare diseases.
• Great Ormond Street Hospital (Gosh) and LifeArc are leading the initiative, in collaboration with the Children’s Hospital Alliance (CHA).
• KidsRare will provide researchers with access to data from various hospitals on young patients with rare conditions.
• The initiative aims to harness existing NHS data to drive research breakthroughs and establish the UK as a global leader in rare disease research and care.
• Families, such as Francesca Granata-Tyler's, whose daughter received a diagnosis thanks to data access, welcome the platform, hoping it will provide earlier diagnoses and potential new treatments for more children.

IN FULL

Millions of children with rare diseases set to benefit from faster diagnosis and better treatments