
The United States Food and Drug Administration (FDA) has awarded Rare Pediatric Disease Designation (RPDD) to Kazia Therapeutics’ (NASDAQ:KZIA) lead drug Paxalisib for the treatment of atypical rhabdoid / teratoid tumors (AT/RT).
AT/RT is a rare and highly-aggressive childhood brain cancer, most common cause of cancer death in children, and outcomes in many forms of childhood brain cancer have not improved in decades.