A company called uniQure has announced promising results from a trial of a new gene therapy for Huntington’s disease. The news has spread quickly through families affected by this condition, who have been desperately waiting for a treatment that can stop or slow down this devastating illness.
Huntington’s disease is a fatal brain disorder that runs in families, caused by a faulty gene that produces a protein called huntingtin. The disease typically begins to cause symptoms in people between 30 and 50 years old.
