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Benzinga
Benzinga
Technology
Ragothaman Srinivasan

BridgeBio Pharma Reveals Early Positive Data For Canavan Disease

Disease BridgeBio Pharma

BridgeBio Pharma (NASDAQ:BBIO) announced early positive data from the the first two participants dosed in CANaspire clinical study for the treatment of Canavan disease.

CANaspire is a Phase 1/2 open-label study designed to evaluate the safety, tolerability, and pharmacodynamic activity of AAV9 gene therapy candidate, BBP-812, for the treatment of Canavan disease.

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